L
L. Mehta
Researcher at Icahn School of Medicine at Mount Sinai
Publications - 1
Citations - 261
L. Mehta is an academic researcher from Icahn School of Medicine at Mount Sinai. The author has contributed to research in topics: Alglucosidase alfa & Population. The author has an hindex of 1, co-authored 1 publications receiving 240 citations.
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Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease
Marc Nicolino,Barry J. Byrne,James E. Wraith,Nancy D. Leslie,Hanna Mandel,David R. Freyer,Georgianne L. Arnold,Eniko K. Pivnick,C. J. Ottinger,Peter H. Robinson,John Charles A Loo,Martin Smitka,Philip Jardine,Luciano Tatò,Brigitte Chabrol,Shawn E. McCandless,Shigemi Kimura,L. Mehta,Deeksha Bali,Alison Skrinar,Claire Morgan,Lakshmi Rangachari,Deya Corzo,Priya S. Kishnani +23 more
TL;DR: In this population of infants with advanced disease, biweekly infusions with alglucosidase alfa prolonged survival and invasive ventilation-free survival and improved indices of cardiomyopathy, motor skills, and functional independence.