A
Allison A Morgan
Publications - 1
Citations - 279
Allison A Morgan is an academic researcher. The author has contributed to research in topics: Placebo & Drisapersen. The author has an hindex of 1, co-authored 1 publications receiving 262 citations.
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Safety and efficacy of drisapersen for the treatment of Duchenne muscular dystrophy (DEMAND II): an exploratory, randomised, placebo-controlled phase 2 study.
Thomas Voit,Haluk Topaloglu,Volker Straub,Francesco Muntoni,Nicolas Deconinck,Giles G Campion,Sjef J. de Kimpe,Michelle Eagle,Michela Guglieri,Steve S Hood,Lia Liefaard,Afrodite Lourbakos,Allison A Morgan,Joanna Nakielny,Naashika Quarcoo,Valeria Ricotti,Katie Rolfe,Laurent Servais,C. Wardell,Rosamund Wilson,Padraig Wright,Padraig Wright,John E. Kraus +22 more
TL;DR: Continuous drisapersen resulted in some benefit in 6MWD versus placebo at week 25 in patients in the intention-to-treat population for whom data were available, andAmbulation improvements in this young population with early-stage Duchenne muscular dystrophy are encouraging but need to be confirmed in larger studies.