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Artur V. Cideciyan

Researcher at University of Pennsylvania

Publications -  284
Citations -  23109

Artur V. Cideciyan is an academic researcher from University of Pennsylvania. The author has contributed to research in topics: Retinal degeneration & Retina. The author has an hindex of 82, co-authored 275 publications receiving 20805 citations. Previous affiliations of Artur V. Cideciyan include University of Florida & Scheie Eye Institute.

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Gene therapy restores vision in a canine model of childhood blindness.

TL;DR: The results indicate that visual function was restored in this large animal model of childhood blindness, and gene therapy directed at photoreceptors and RPE in a large-animal model of human disease has not been reported.
Journal ArticleDOI

Treatment of Leber Congenital Amaurosis Due to RPE65 Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results of a Phase I Trial

TL;DR: A recombinant adeno-associated virus serotype 2 vector, altered to carry the human RPE65 gene (rAAV2-CBSB-hRPE65) restored vision in animal models with R PE65 deficiency, and Comparisons are drawn between the present work and two other studies of ocular gene therapy for RPE 65-LCA that were carried out contemporaneously and reported.