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Marcy E. MacDonald

Researcher at Harvard University

Publications -  322
Citations -  52277

Marcy E. MacDonald is an academic researcher from Harvard University. The author has contributed to research in topics: Huntington's disease & Huntingtin. The author has an hindex of 96, co-authored 315 publications receiving 49085 citations. Previous affiliations of Marcy E. MacDonald include Huntington's Disease Society of America & Ontario Institute for Cancer Research.

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Cln3(Deltaex7/8) knock-in mice with the common JNCL mutation exhibit progressive neurologic disease that begins before birth.

TL;DR: The harmful impact of the common JNCL mutation on the CNS was not well correlated with membrane deposition per se, suggesting instead a specific battenin activity that is essential for the survival of CNS neurons.
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Single sperm analysis of the trinucleotide repeats in the Huntington's disease gene: quantification of the mutation frequency spectrum

TL;DR: The CAG triplet repeat region of the Huntington's disease gene was amplified in 923 single sperm from three affected and two normal individuals and an excellent fit was found when the model specified that a random number of repeats are added during the progression of the polymerase through the repeated region.
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Reversal of a full-length mutant huntingtin neuronal cell phenotype by chemical inhibitors of polyglutamine-mediated aggregation.

TL;DR: At least some compounds identified as aggregation inhibitors also prevent a neuronal cellular phenotype caused by full-length mutant huntingtin, suggesting that in vitro fragment aggregation can act as a proxy for monitoring the disease-producing conformational property in HD.
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Biotin-responsive Basal Ganglia Disease Maps to 2q36.3 and Is Due to Mutations in SLC19A3

TL;DR: Using linkage analysis in four families, the genetic defect near marker D2S2158 in 2q36 was mapped to a minimum candidate region (approximately 2 Mb) between D 2S2354 and D2 S1256, on the basis of complete homozygosity.