L
Luigi Naldini
Researcher at Vita-Salute San Raffaele University
Publications - 370
Citations - 59320
Luigi Naldini is an academic researcher from Vita-Salute San Raffaele University. The author has contributed to research in topics: Genetic enhancement & Viral vector. The author has an hindex of 108, co-authored 345 publications receiving 55080 citations. Previous affiliations of Luigi Naldini include Università telematica San Raffaele & Sangamo BioSciences.
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1038. Lentiviral Gene Transfer into HSC Is Enhanced by Early-Acting Cytokines without Impairing Stem Cell Properties and Involves Cellular Responses Distinct from Cell Cycle Control
TL;DR: Preliminary results rather indicate that, in hematopoietic progenitors, susceptibility to LV transduction is differentially regulated by the activity of a specific enzymatic complex in the cytosol, and that interference with this system strongly up-regulates transduction efficiency.
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CTIM-24. AUTOLOGOUS CD34+ ENRICHED HEMATOPOIETIC PROGENITOR CELLS GENETICALLY MODIFIED FOR HUMAN INTERFERON-α2, ARE WELL TOLERATED & RAPIDLY ENGRAFT IN PATIENTS WITH GLIOBLASTOMA MULTIFORME (TEM-GBM_001 STUDY)
Gaetano Finocchiaro,Bernhard Gentner,Marica Eoli,Farina Francesca,Elena Anghileri,Stefania Girlanda,Matteo Carrabba,Valeria Cuccarini,Francesco DiMeco,Federico G. Legnani,Bianca Pollo,Maria Grazia Bruzzone,Marco Saini,Paolo Ferroli,Alessia Capotondo,Rosina Paterra,Mariagrazia Garramone,Stefania Mazzoleni,Andrew Zambanini,Carlo Russo,Luigi Naldini,Fabio Ciceri +21 more
TL;DR: Preliminary results indicate feasibility of engrafting a pre-determined fraction of Temferon cells in the bone marrow of GBM patients without, so far, causing dose-limiting toxicity.
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OS05.6.A Modification of the tumor microenvironment in patients with glioblastoma using autologous, genetically modified, hematopoietic stem cell-based therapy: the TEM-GBM STUDY (NCT03866109)
Giovanna Finocchiaro,Marica Eoli,Bernhard Gentner,M. G. Bruzzone,Francesco DiMeco,Pietro Mortini,A Olivi,Luigi Naldini,C. Russo,Fabio Ciceri +9 more
TL;DR: Initial evidence of Temferon’s potential to modulate the TME of GBM patients, and anecdotal evidence for long lasting effects ofTemferon in prevention of disease progression are provided.
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Long-term efficacy and safety of hematopoietic stem cell gene therapy mediated by lentiviral vectors in the murine model of Wiskott-Aldrich syndrome
Marita Bosticardo,Francesco Marangoni,Michela Locci,Elena Draghici,Samantha Scaramuzza,Cristina Panaroni,Anne Galy,Luigi Naldini,Alessandro Aiuti,Loïc Dupré,Maria Grazia Roncarolo,Anna +11 more