A
Andrea Swenson
Researcher at University of Iowa
Publications - 42
Citations - 2027
Andrea Swenson is an academic researcher from University of Iowa. The author has contributed to research in topics: Medicine & Randomized controlled trial. The author has an hindex of 15, co-authored 37 publications receiving 1135 citations. Previous affiliations of Andrea Swenson include Veterans Health Administration & University of Iowa Hospitals and Clinics.
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Journal ArticleDOI
Genome-wide Analyses Identify KIF5A as a Novel ALS Gene.
Aude Nicolas,Kevin P. Kenna,Alan E. Renton,Alan E. Renton,Nicola Ticozzi,Faraz Faghri,Faraz Faghri,Ruth Chia,Janice A. Dominov,Brendan J. Kenna,Mike A. Nalls,Pamela Keagle,Alberto M. Rivera,Wouter van Rheenen,Natalie A. Murphy,Joke J.F.A. van Vugt,Joshua T. Geiger,Rick A.A. van der Spek,Hannah A. Pliner,Shankaracharya,Bradley N. Smith,Giuseppe Marangi,Giuseppe Marangi,Simon Topp,Yevgeniya Abramzon,Yevgeniya Abramzon,Athina Soragia Gkazi,John D. Eicher,Aoife Kenna,Francesco Logullo,Isabella Simone,Giancarlo Logroscino,Fabrizio Salvi,Ilaria Bartolomei,Giuseppe Borghero,Maria Rita Murru,Emanuela Costantino,Carla Pani,Roberta Puddu,Carla Caredda,Valeria Piras,Stefania Tranquilli,Stefania Cuccu,Daniela Corongiu,Maurizio Melis,Antonio Milia,Francesco Marrosu,Maria Giovanna Marrosu,Gianluca Floris,Antonino Cannas,Margherita Capasso,Claudia Caponnetto,Gianluigi Mancardi,Paola Origone,Paola Mandich,Francesca Luisa Conforti,Sebastiano Cavallaro,Gabriele Mora,Kalliopi Marinou,Riccardo Sideri,Silvana Penco,Lorena Mosca,Christian Lunetta,Giuseppe Lauria Pinter,Massimo Corbo,Nilo Riva,Paola Carrera,Paolo Volanti,Jessica Mandrioli,Nicola Fini,Antonio Fasano,Lucio Tremolizzo,A Arosio,Carlo Ferrarese,Francesca Trojsi,Gioacchino Tedeschi,Maria Rosaria Monsurrò,Giovanni Piccirillo,Cinzia Femiano,Anna Ticca,Enzo Ortu,Vincenzo La Bella,Rossella Spataro,Tiziana Colletti,Mario Sabatelli,Marcella Zollino,Amelia Conte,Marco Luigetti,Serena Lattante,Marialuisa Santarelli,Antonio Petrucci,Maura Pugliatti,Angelo Pirisi,Leslie D. Parish,Patrizia Occhineri,Fabio Giannini,Stefania Battistini,Claudia Ricci,Michele Benigni,Tea B. Cau,Daniela Loi,Andrea Calvo,Cristina Moglia,Maura Brunetti,Marco Barberis,Gabriella Restagno,Federico Casale,Giuseppe Marrali,Giuseppe Fuda,Irene Ossola,Stefania Cammarosano,Antonio Canosa,Antonio Ilardi,Umberto Manera,Maurizio Grassano,Raffaella Tanel,Fabrizio Pisano,Letizia Mazzini,Sonia Messina,Isabella Laura Simone,Sandra D'Alfonso,Lucia Corrado,Luigi Ferrucci,Matthew B. Harms,David Goldstein,Neil A. Shneider,Stephen A. Goutman,Zachary Simmons,Timothy M. Miller,Siddharthan Chandran,Suvankar Pal,George Manousakis,Stanley H. Appel,Ericka Simpson,Leo H. Wang,Robert H. Baloh,Summer B. Gibson,Richard Bedlack,David Lacomis,Dhruv Sareen,Alexander Sherman,Lucie Bruijn,Michelle Penny,Cristiane de Araújo Martins Moreno,Sitharthan Kamalakaran,Andrew S. Allen,Stanley Appel,Richard S. Bedlack,Braden E. Boone,Robert H. Brown,John P. Carulli,Alessandra Chesi,Wendy K. Chung,Elizabeth T. Cirulli,Gregory M. Cooper,Julien Couthouis,Aaron G. Day-Williams,Patrick A. Dion,Aaron D. Gitler,Jonathan D. Glass,Yujun Han,Timothy D. Harris,Sebastian D. Hayes,Angela Jones,Jonathan Keebler,Brian J. Krueger,Brittany N. Lasseigne,Shawn Levy,Yi-Fan Lu,Tom Maniatis,Diane McKenna-Yasek,Richard M. Myers,Slavé Petrovski,Stefan M. Pulst,Alya R. Raphael,John M. Ravits,Zhong Ren,Guy A. Rouleau,Peter C. Sapp,Katherine B. Sims,John F. Staropoli,Lindsay L. Waite,Quanli Wang,Jack R. Wimbish,Winnie Xin,Hemali Phatnani,Justin Y. Kwan,James R. Broach,Ximena Arcila-Londono,Edward B. Lee,Vivianna M. Van Deerlin,Ernest Fraenkel,Lyle W. Ostrow,Frank Baas,Noah Zaitlen,James D. Berry,Andrea Malaspina,Pietro Fratta,Gregory A. Cox,Leslie M. Thompson,Steve Finkbeiner,Efthimios Dardiotis,Eran Hornstein,Daniel MacGowan,Terry Heiman-Patterson,Molly G. Hammell,Nikolaos A. Patsopoulos,Joshua Dubnau,Avindra Nath,Rajeeva Musunuri,Uday S. Evani,Avinash Abhyankar,Michael C. Zody,Julia A. Kaye,Steven Finkbeiner,Stacia K. Wyman,Alexander LeNail,Leandro Lima,Jeffrey D. Rothstein,Clive N. Svendsen,Jenny Van Eyk,Nicholas J. Maragakis,Stephen J. Kolb,Merit Cudkowicz,Emily G. Baxi,Stacia Wyman,Alex LeNail,Jennifer E. Van Eyk,Michael Benatar,J. Paul Taylor,Gang Wu,Evadnie Rampersaud,Joanne Wuu,Rosa Rademakers,Stephan Züchner,Rebecca Schüle,Jacob L. McCauley,Sumaira Hussain,Anne Cooley,Marielle Wallace,Christine Clayman,Richard J. Barohn,Jeffrey Statland,John Ravits,Andrea Swenson,Carlayne E. Jackson,Jaya Trivedi,Shaida Khan,Jonathan L. Katz,Liberty Jenkins,Ted M. Burns,Kelly G. Gwathmey,James Caress,Corey T. McMillan,Lauren Elman,Erik P. Pioro,Jeannine M. Heckmann,Yuen T. So,David Walk,Samuel Maiser,Jinghui Zhang,Vincenzo Silani,C. Gellera,Antonia Ratti,Franco Taroni,Giuseppe Lauria,Federico Verde,Isabella Fogh,Cinzia Tiloca,Giacomo P. Comi,Gianni Sorarù,Cristina Cereda,Fabiola De Marchi,Stefania Corti,Mauro Ceroni,Gabriele Siciliano,Massimiliano Filosto,Maurizio Inghilleri,Silvia Peverelli,Claudia Colombrita,Barbara Poletti,Luca Maderna,Roberto Del Bo,Stella Gagliardi,Giorgia Querin,Cinzia Bertolin,Viviana Pensato,Barbara Castellotti,William Camu,Kevin Mouzat,Serge Lumbroso,Philippe Corcia,Vincent Meininger,Gérard Besson,Emmeline Lagrange,Pierre Clavelou,Nathalie Guy,Philippe Couratier,Patrick Vourc'h,Veronique Danel,Emilien Bernard,Gwendal Lemasson,Hannu Laaksovirta,Liisa Myllykangas,Lilja Jansson,Miko Valori,John Ealing,Hisham Hamdalla,Sara Rollinson,Stuart Pickering-Brown,Richard W. Orrell,Katie C. L. Sidle,John Hardy,Andrew B. Singleton,Janel O. Johnson,Sampath Arepalli,Meraida Polak,Seneshaw Asress,Safa Al-Sarraj,Andrew T. King,Claire Troakes,Caroline Vance,Jacqueline de Belleroche,Anneloor L.M.A. ten Asbroek,José Luis Muñoz-Blanco,Dena G. Hernandez,Jinhui Ding,J. Raphael Gibbs,Sonja W. Scholz,Mary Kay Floeter,Roy H. Campbell,Francesco Landi,Robert Bowser,Daniel J. L. MacGowan,Janine Kirby,Erik P. Pioro,Roger Pamphlett,James Broach,Glenn S. Gerhard,Travis Dunckley,Christopher B. Brady,Christopher B. Brady,Neil W. Kowall,Juan C. Troncoso,Isabelle Le Ber,Terry Heiman-Patterson,Terry Heiman-Patterson,Freya Kamel,Ludo Van Den Bosch,Tim M. Strom,Thomas Meitinger,Aleksey Shatunov,Kristel R. van Eijk,Mamede de Carvalho,Maarten Kooyman,Bas Middelkoop,Matthieu Moisse,Russell L. McLaughlin,Michael A. van Es,Markus Weber,Kevin B. Boylan,Marka van Blitterswijk,Karen E. Morrison,A. Nazli Basak,Jesus S. Mora,Vivian E. Drory,Pamela J. Shaw,Martin R Turner,Kevin Talbot,Orla Hardiman,Kelly L. Williams,Jennifer A. Fifita,Garth A. Nicholson,Garth A. Nicholson,Ian P. Blair,Jesús Esteban-Pérez,Alberto García-Redondo,Ammar Al-Chalabi,Ahmad Al Kheifat,Peter M. Andersen,Adriano Chiò,Jonathan Cooper-Knock,Annelot M. Dekker,Vivian E. Drory,Alberto Garcia Redondo,Marc Gotkine,Winston Hide,Alfredo Iacoangeli,Jonathan Glass,K.P. Kenna,Matthew C. Kiernan,John E. Landers,Russell McLaughlin,Jonathan Mill,Miguel Mitne Neto,Mattieu Moisse,Jesus S. Mora Pardina,Karen E. Morrison,Stephen Newhouse,Susana Pinto,Sara L. Pulit,Wim Robberecht,Pamela Shaw,Chris Shaw,William Sproviero,Gijs H.P. Tazelaar,Philip Van Damme,Leonard H. van den Berg,Rick van der Spek,Kristel R van Eijk,Michael A van Es,Joke van Vugt,J. H. Veldink,Mayana Zatz,Denis C. Bauer,Natalie A. Twine,Ekaterina Rogaeva,Lorne Zinman,Johnathan Cooper-Knock,Alexis Brice,Stephen A. Goutman,Eva L. Feldman,Summer Gibson,Albert C. Ludolph,Peter M Andersen,Jochen H. Weishaupt,John Q. Trojanowski,Robert H. Brown,Leonard H. van den Berg,Jan H. Veldink,David J. Stone,Pentti J. Tienari,Christopher Shaw,Bryan J. Traynor,Bryan J. Traynor,John Landers +435 more
TL;DR: Interestingly, mutations predominantly in the N-terminal motor domain of KIF5A are causative for two neurodegenerative diseases: hereditary spastic paraplegia and Charcot-Marie-Tooth type 2.
Journal ArticleDOI
Safety and efficacy of eculizumab in anti-acetylcholine receptor antibody-positive refractory generalised myasthenia gravis (REGAIN): a phase 3, randomised, double-blind, placebo-controlled, multicentre study
James F. Howard,Kimiaki Utsugisawa,Michael Benatar,Hiroyuki Murai,Richard J. Barohn,Isabel Illa,Saiju Jacob,John Vissing,Ted M. Burns,John T. Kissel,Srikanth Muppidi,Richard Nowak,Fanny O'Brien,Jing Jing Wang,Renato Mantegazza,Claudio Mazia,Miguel Wilken,Carolina Ortea,Juliet Saba,Marcelo Rugiero,Mariela Bettini,Gonzalo Vidal,Alejandra Dalila Garcia,Phillipa Lamont,Wai-Kuen Leong,Heidi Boterhoven,Beverly Fyfe,Leslie Roberts,Mahi Jasinarachchi,Natasha Willlems,Julia Wanschitz,Wolfgang Löscher,Jan De Bleecker,Guy Van den Abeele,Kathy de Koning,Katrien De Mey,Rudy Mercelis,Linda Wagemaekers,Delphine Mahieu,Philip Van Damme,Charlotte Smetcoren,Olivier Stevens,Sarah Verjans,Ann D'Hondt,Petra Tilkin,Alzira Alves de Siqueira Carvalho,Rosa Hasan,Igor Dias Brockhausen,David Feder,Daniel Ambrosio,Ana Paula Melo,Rosana Rocha,Bruno Bezerra Rosa,Thabata Veiga,Luiz Augusto da Silva,Jordana Gonçalves Geraldo,Maria da Penha Morita Ananias,Erica Nogueira Coelho,Gabriel Paiva,Marina Pozo,Natalia Prando,Debora Dada Martineli Torres,Cristiani Fernanda Butinhao,Erica Coelho,Luciana Renata Cubas Volpe,Gustavo Duran,Tamires Cristina Gomes da Silva,Luiz Otavio Maia Gonçalves,Lucas Eduardo Pazetto,Luciana Souza Duca,Tomás Augusto Suriane Fialho,Maurício André Gheller Friedrich,Alexandre Guerreiro,Henrique Mohr,Maurer Pereira Martins,Daiane da Cruz Pacheco,Ana Paula Macagnan,Aline de Cassia Santos,Acary Souza Bulle Oliveira,Ana Carolina Amaral de Andrade,Marcelo Annes,Valeria Cavalcante Lino,Wladimir Bocca Vieira de Rezende Pinto,Carolina Miranda,Fernanda Carrara,Iandra Souza,Angela Genge,Rami Massie,Natasha Campbell,Vera Bril,Hans D. Katzberg,Mehran Soltani,Eduardo Ng,Zaeem A. Siddiqi,Celile Phan,Derrick Blackmore,Stanislav Vohanka,Josef Bednarik,Magda Chmelikova,Marek Čierny,Stanislava Toncrova,Jana Junkerova,Barbora Kurkova,Katarina Reguliova,Olga Zapletalova,Jiri Pitha,Iveta Novakova,Michaela Tyblova,Marcela Wolfova,Ivana Jurajdova,Henning Andersen,Thomas Harbo,Lotte Vinge,Anita Mogensen,Joan Højgaard,Nanna Witting,Anne Mette Ostergaard Autzen,Jane Pedersen,Markus Färkkilä,Sari Atula,Anne Nyrhinen,Juha-Pekka Erälinna,Mikko Laaksonen,Olli Oksaranta,Jaana Eriksson,Tuula Harrison,Claude Desnuelle,Sabrina Sacconi,Marie-Hélène Soriani,Sonia Decressac,Julie Moutarde,Pauline Lahaut,Guilhem Sole,Gwendal Le Masson,Anne-Cécile Wielanek-Bachelet,Morgane Gaboreau,Caroline Moreau,Amy Wilson,Christophe Vial,Francoise Bouhour,Helene Gervais-Bernard,Hélène Merle,Caroline Hourquin,Arnaud Lacour,Olivier Outteryck,Patrick Vermersch,Hélène Zéphir,Edouard Millois,Michel Deneve,Fabienne Deruelle,Benedikt Schoser,Stephan Wenninger,Martin Stangel,Sascha Alvermann,Stefan Gingele,Thomas Skripuletz,Kurt-Wolfram Suehs,C. Trebst,Karin Fricke,Sotirios Papagiannopoulos,Sevasti Bostantzopoulou,Nicholas Vlaikidis,Martha Zampaki,Nikoletta Papadopoulou,Dimos-Dimitrios Mitsikostas,Eleni Kasioti,Efstathia Mitropoulou,Despoina Charalambous,Csilla Rozsa,Melinda Horvath,Gabor Lovas,Judit Matolcsi,Gyorgyi Szabo,Brigitta Szabadosne,László Vécsei,Livia Dezsi,Edina Varga,Monika Konyane,Bella Gross,Olga Azrilin,Nelly Greenbereg,Hila Bali Kuperman,Giovanni Antonini,Matteo Garibaldi,Stefania Morino,Fernanda Troili,Antonella Di Pasquale,Alessandro Filla,Teresa Costabile,Enrico Marano,Francesco Saccà,Angela Marsil,Giorgia Puorro,Michelangelo Maestri Tassoni,Anna De Rosa,Silvia Bonanno,Carlo Antozzi,Lorenzo Maggi,Angela Campanella,Corrado Angelini,Paola Cudia,Valentina Pegoraro,Elena Pinzan,Francesca Bevilacqua,Daniele Orrico,Domenico Marco Bonifati,Amelia Evoli,Paolo Emilio Alboini,Valentina Damato,Raffaele Iorio,Maurizio Inghilleri,Laura Fionda,Vittorio Frasca,Elena Giacomelli,Maria Cristina Gori,Diego Lopergolo,Emanuela Onesti,Maria Gabriele,Francesco Patti,Andrea Caramma,Silvia Messina,Ester Reggio,Cinzia Caserta,Akiyuki Uzawa,Tetsuya Kanai,Masahiro Mori,Yoko Kaneko,Akiko Kanzaki,Eri Kobayashi,Katsuhisa Masaki,Dai Matsuse,Takuya Matsushita,Taira Uehara,Misa Shimpo,Maki Jingu,Keiko Kikutake,Yumiko Nakamura,Yoshiko Sano,Yuriko Nagane,Ikuko Kamegamori,Yuko Fujii,Kazumi Futono,Tomoko Tsuda,Yuka Saito,Hidekazu Suzuki,Miyuki Morikawa,Makoto Samukawa,Sachiko Kamakura,Hirokazu Shiraishi,Teiichiro Mitazaki,Masakatsu Motomura,Akihiro Mukaino,Shunsuke Yoshimura,Shizuka Asada,Tomomi Kobashikawa,Megumi Koga,Yasuko Maeda,Kazumi Takada,Mihoko Takada Takada,Yumi Yamashita,Seiko Yoshida,Yasushi Suzuki,Tetsuya Akiyama,Koichi Narikawa,Kenichi Tsukita,Fumie Meguro,Yusuke Fukuda,Miwako Sato,Hidenori Matsuo,Takayasu Fukudome,Yuichiro Gondo,Yasuhiro Maeda,Akiko Nagaishi,Shunya Nakane,Yoshinori Okubo,Meinoshin Okumura,Soichiro Funaka,Tomohiro Kawamura,Masayuki Makamori,Masanori Takahashi,Tomoya Hasuike,Eriko Higuchi,Hisako Kobayashi,Kaori Osakada,Namie Taichi,Emiko Tsuda,Takashi Hayashi,Shin Hisahara,Tomihiro Imai,Jun Kawamata,Takashi Murahara,Masaki Saitoh,Shun Shimohama,Shuichiro Suzuki,Daisuke Yamamoto,Shingo Konno,Tomomi Imamura,Masashi Inoue,Mayumi Murata,Hiroshi Nakazora,Ritsu Nakayama,Yasuko Ikeda,Miki Ogawa,Maoko Shirane,Takashi Kanda,M. Kawai,Michiaki Koga,Junichi Ogasawara,Masatoshi Omoto,Yasuteru Sano,Hideki Arima,Sachie Fukui,Shigemi Shimose,Hirokazu Shinozaki,Masanori Watanabe,Chieko Yoshikawa,Anneke J. van der Kooi,Marianne de Visser,Tamar Gibson,Jos Maessen,Marc H. De Baets,Catherine Faber,Maria Johanna Keijzers,Monique Miesen,Anna Kostera-Pruszczyk,Anna Kaminska,Byung Jo Kim,Chang Nyoung Lee,Yong Seo Koo,Hung Youl Seok,Hoo Nam Kang,HyeJin Ra,Byoung Joon Kim,Eun Bin Cho,HyeLim Lee,Ju-Hong Min,Jinmyoung Seok,Da Yoon Koh,JuYoung Kwon,Ji Eun Lee,SangAe Park,Yoon-Ho Hong,Jae-Sung Lim,Miri Kim,Seung Min Kim,Yool-hee Kim,Hyung Seok Lee,Ha Young Shin,Eun Bi Hwang,Miju Shin,Denis Sazonov,Asya Yarmoschuk,Larisa Babenko,Nadezhda Malkova,Anna Melnikova,Denis Korobko,Evgeniya Kosykh,Dmitry Pokhabov,Yulia Nesterova,Vladislav Abramov,Victor Balyazin,Carlos Casasnovas Pons,Maria Antonia Alberti Aguilo,Christian Homedes-Pedret,Natalia Julia Palacios,Ana Lazaro,Exuperio Diez Tejedor,Mireya Fernandez-Fournier,Pedro Lopez Ruiz,Francisco Javier Rodriguez de Rivera,Maria Salvado Figueras,Josep Gamez,Maria Salvado,Elena Cortes Vicente,Jordi Díaz-Manera,Luis Antonio Querol Gutierrez,Ricardo Rojas Garcia,Nuria Vidal,Elisabet Arribas-Ibar,Fredrik Piehl,Albert Hietala,Lena Bjarbo,Christopher Lindberg,Daniel Jons,Blanka Andersson,Ihsan Sengun,Pinar Ozcelik,Celal Tuga,Muzeyyen Ugur,Cavit Boz,Didem Altiparmak,Sibel Gazioglu,Cigdem Ozen Aydin,Sevim Erdem-Ozdamar,Can Ebru Bekircan-Kurt,Ezgi Yilmaz,Nazire Pinar Acar,Yagmur Caliskan,Husnu Efendi,Seda Aydinlik,Hakan Cavus,Cansu Semiz,Ozlem Tun,Murat Terzi,Baki Dogan,Musa Kazim Onar,Sedat Sen,Tugce Kirbas Cavdar,Fiona Norwood,Aikaterini Dimitriou,Jakit Gollogly,Mohamed Mahdi-Rogers,Arshira Seddigh,Gal Maier,Faisal Sohail,Sivakumar Sathasivam,Heike Arndt,Debbie Davies,Dave Watling,Michael H. Rivner,J. Edward Hartmann,Brandy Quarles,Nicole Smalley,Anthony A. Amato,Thomas Cochrane,Mohammed Salajegheh,Kristen Roe,Katherine Amato,Shirli Toska,Gil I. Wolfe,Nicholas Silvestri,Kara Patrick,Karen Zakalik,Jonathan S. Katz,Robert G. Miller,Marguerite Engel,Elena Bravver,Benjamin Rix Brooks,Sarah Plevka,Maryanne Burdette,Mohammad Sanjak,Megan Kramer,Joanne Nemeth,Clara Schommer,Vern C. Juel,Jeffrey T. Guptill,Lisa D. Hobson-Webb,Kate Beck,Donna Carnes,John Loor,Amanda Anderson,Dale J. Lange,Eliz Agopian,Jonathan Goldstein,Erin Manning,Lindsay Kaplan,Shara Holzberg,Nicole Kassebaum,Robert M. Pascuzzi,Cynthia Bodkin,John C. Kincaid,Riley Snook,Sandra Guinrich,Angela Micheels,Vinay Chaudhry,Andrea M. Corse,Betsy Mosmiller,Doreen Ho,Jayashri Srinivasan,Michael Vytopil,Nicholas Ventura,Stephanie Scala,Cynthia Carter,Craig Donahue,Carol Herbert,Elaine Weiner,Jonathan McKinnon,Laura Haar,Naya McKinnon,Karan Alcon,Kevin Daniels,Nadia Sattar,Dennis Jeffery,Kaitlyn McKenna,Amanda C. Guidon,William S. David,Christina Dheel,Mark Levine-Weinberg,Catherine Nigro,Ericka Simpson,Stanley H. Appel,Eugene Lai,Luis Lay,Milvia Pleitez,Sharon Halton,Casey Faigle,Lisa Thompson,Mark Sivak,Susan Shin,Joan Bratton,Daniel Jacobs,Gavin Brown,Ibrez Bandukwala,Morris Brown,Jennifer Kane,Ira Blount,Miriam Freimer,J. Chad Hoyle,Julie Agriesti,Julie Khoury,Tessa Marburger,Harpreet Kaur,Diana Dimitrova,Michelle Mellion,George Sachs,Brigid Crabtree,Roseann Keo,Ele Kim Perez,Sandra Taber,James Gilchrist,Angela Andoin,Taylor Darnell,Neelam Goyal,Sarada Sakamuri,Yuen T. So,Lesly Welsh,Ratna Bhavaraju-Sanka,Alejandro Tobon Gonzalez,Floyd Jones,Amy Saklad,Sharon P. Nations,Jaya Trivedi,Steve Hopkins,Mohamed Kazamel,Mohammad Alsharabati,Liang Lu,Sandi Mumfrey-Thomas,Amy Woodall,David P. Richman,Janelle Butters,Molly Lindsay,Tahseen Mozaffar,Tiyonnoh Cash,Namita Goyal,Gulmohor Roy,Veena Mathew,Fatima Maqsood,Brian Minton,H. James Jones,Jeffrey V. Rosenfeld,Rebekah Garcia,Sonia Garcia,Laura Echevarria,Michael Pulley,Shachie Aranke,Alan R. Berger,Jaimin Shah,Yasmeen Shabbir,Lisa Smith,Mary Varghese,Laurie Gutmann,Ludwig Gutmann,Andrea Swenson,Heena Olalde,Charlene Hafer-Macko,Justin Y. Kwan,Lindsay Zilliox,Karen Callison,Beth DiSanzo,Kerry Naunton,Martin Bilsker,Khema Sharma,Eliana Reyes,Anne Cooley,Sara-Claude Michon,Julie Steele,Chafic Karam,Manisha Chopra,Shawn J. Bird,Jacob Kaufman,Nichole Gallatti,Tuan Vu,Lara Katzin,Terry McClain,Brittany Harvey,Adam Hart,Kristin Huynh,Said R. Beydoun,Amaiak Chilingaryan,Brian Droker,Frank Lin,Akshay Shah,Anh Tran,Salma Akhter,Ali Malekniazi,Rup Tandan,Michael K. Hehir,Waqar Waheed,Shannon Lucy,Michael D. Weiss,Jane Distad,Sharon Downing,Susan Strom,Robert P. Lisak,Evanthia Bernitsas,Omar Khan,Shitiz Kumar Sriwastava,Alexandros Tselis,Kelly Jia,Tulio E. Bertorini,Thomas Arnold,Kendrick Henderson,Rekha Pillai,Ye Liu,Lauren Wheeler,Jasmine Hewlett,Mollie Vanderhook,Daniel DiCapua,Benison Keung,Aditya Kumar,Huned S. Patwa,Kimberly Robeson,Joan Nye,Hong Vu +623 more
TL;DR: A phase 3, randomised, double-blind, placebo-controlled, multicentre study in 76 hospitals and specialised clinics across North America, Latin America, Europe, and Asia to assess the efficacy and safety of eculizumab in patients with refractory myasthenia gravis.
Journal ArticleDOI
Trial of Sodium Phenylbutyrate–Taurursodiol for Amyotrophic Lateral Sclerosis
Sabrina Paganoni,Eric A. Macklin,Suzanne Hendrix,James D. Berry,Michael A. Elliott,Samuel Maiser,Chafic Karam,James B. Caress,Margaret A. Owegi,Adam Quick,James Wymer,Stephen A. Goutman,Daragh Heitzman,Terry Heiman-Patterson,Carlayne E. Jackson,Colin Quinn,Jeffrey D. Rothstein,Edward J. Kasarskis,Jonathan S. Katz,Liberty Jenkins,Shafeeq Ladha,Timothy M. Miller,Stephen N. Scelsa,Tuan Vu,Christina Fournier,Jonathan D. Glass,Kristin M. Johnson,Andrea Swenson,Namita Goyal,Gary L. Pattee,Patricia L. Andres,Suma Babu,Marianne Chase,Derek Dagostino,Samuel P. Dickson,Noel Ellison,Meghan Hall,Kent Allen Hendrix,Gale Kittle,Michelle McGovern,Joseph Ostrow,Lindsay Pothier,Rebecca Randall,Jeremy M. Shefner,Alexander Sherman,Eric Tustison,Prasha Vigneswaran,Jason Walker,Hong Yu,James Chan,Janet Wittes,Joshua D. Cohen,Justin Klee,Kent L. Leslie,Rudolph E. Tanzi,Walter Gilbert,Patrick D. Yeramian,David A. Schoenfeld,Merit Cudkowicz +58 more
TL;DR: Sodium phenylbutyrate-taurursodiol resulted in slower functional decline than placebo as measured by the ALSFRS-R score over a period of 24 weeks, and was found to reduce neuronal death in experimental models.
Journal ArticleDOI
A randomized controlled trial of methotrexate for patients with generalized myasthenia gravis
Mamatha Pasnoor,Jianghua He,Laura Herbelin,Ted M. Burns,Sharon P. Nations,Vera Bril,Annabel K. Wang,Bakri Elsheikh,John T. Kissel,David Saperstein,J. Aziz Shaibani,Carlayne E. Jackson,Andrea Swenson,James F. Howard,Namita Goyal,William S. David,Matthew Wicklund,Michael Pulley,Mara L. Becker,Tahseen Mozaffar,Michael Benatar,Robert Pazcuzzi,Ericka Simpson,Jeffrey Rosenfeld,Mazen M. Dimachkie,Jeffrey Statland,Richard J. Barohn +26 more
TL;DR: This study demonstrates the challenges of conducting clinical trials in MG, including difficulties with recruitment, participants improving on prednisone alone, and the need for a better understanding of outcome measure variability for future clinical trials.
Journal ArticleDOI
Validation of serum neurofilaments as prognostic and potential pharmacodynamic biomarkers for ALS
Michael Benatar,Lanyu Zhang,Lily Wang,Volkan Granit,Jeffrey Statland,Richard J. Barohn,Andrea Swenson,John Ravits,Carlayne E. Jackson,Ted M. Burns,Jaya Trivedi,Erik P. Pioro,James B. Caress,Jonathan S. Katz,Jacob L. McCauley,Rosa Rademakers,Andrea Malaspina,Lyle W. Ostrow,Joanne Wuu +18 more
TL;DR: Serum NfL may be considered a clinically validated prognostic biomarker for ALS and has potential utility as a pharmacodynamic biomarker of treatment effect, depending on the method used to estimate effect size.